A mosaic of human cells inside Vertex Pharmaceuticals' cell and gene-therapy laboratory.
The four-story, 267,000-square-foot space is home to Vertex's cell and gene-therapy unit, with about 375 people now residing in the modern-industrial building.
That has led to going after unrelated diseases like sickle cell, diabetes, muscular dystrophy, kidney disease, and pain.
For instance, Vertex's approach to sickle cell is led by its CRISPR gene-editing program.
Vertex PharmaceuticalsThe next test of Vertex's strategy will be an experimental treatment called exa-cel, its CRISPR gene-editing program for sickle cell.