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☆ My daughter's disabilities mean I have to stay physically strong. So, I found a personal trainer for caregivers.
▼ + stars: | 2024-10-15 | by ( Claire Mcmurray | ) www.businessinsider.com time to read: +4 min

She will need my help throughout life, so I'm focused on keeping my body strong to be there for her. AdvertisementWhen she was 3, my daughter, JJ, was diagnosed with Rett Syndrome. Normally, I hit the gym six days a week, alternating strength training, running, stationary biking, Pilates, and kickboxing. She watched me lift and carry JJ, corrected my technique, and brainstormed ways to improve the setup in our house. I now had the training and knowledge to push myself, so I began increasing my weights and mixing up my strength training workouts.

Persons: —, JJ, Kayla Lyman, Lyman, twinges Organizations: Service, Rett, Fitness

☆ 'This is the mental health moment': Innovation and M&A are helping to boost these stocks to new heights
▼ + stars: | 2024-02-19 | by ( Michelle Fox | ) www.cnbc.com time to read: +14 min

There's been a lot of chatter about the mental health crisis since the Covid-19 pandemic. Attention to a long-time crisis The mental health crisis is nothing new. However, there has also been a growing awareness and acceptance of mental health illnesses over the past decade, said Canaccord Genuity analyst Richard Close. "There's been recognition that mental health has a significant impact on a person's overall health," he said. "This is the mental health moment," said Dr. Ken Duckworth, NAMI's chief medical officer and author of "You Are Not Alone: The NAMI Guide to Mental Health."

Persons: There's, Covid, Peter Micca, AbbVie, Emraclidine, Myers Squibb, Karuna, Marc Goodman, Canaccord, Richard Close, MacKenzie Scott, Ken Duckworth, NAMI, Deloitte's Micca, William Blair, Myles Minter, Minter, Auvelity, Leerink's Goodman, Ashwani Verma, Verma, Goodman, BioHaven, Cerevel, Neumora, tardive, David Song, BetterHelp, psychedelics Johnson, Johnson, Spravato, Blair's Minter, Axsome, Micca, Michael Bloom Organizations: Institute for Health Metrics, Deloitte, Cerevel Therapeutics, Karuna Therapeutics, Bristol Myers, Leerink Partners, Centers for Disease Control, National Alliance, Mental, Mental Health, Wall Street, Therapeutics, Neumora Therapeutics, UBS, Karuna, Cellular Therapies, Xenon Pharmaceuticals, Neurocrine Biosciences, Acadia Pharmaceuticals, Tema Neuroscience, Axsome Therapeutics, Acadia Healthcare, BetterHelp, CNBC, pharma, Cellular Locations: Covid, Bristol, XEN1101, Acadia, Tema

☆ U.S. FDA approves Acadia's Rett syndrome drug
▼ + stars: | 2023-03-14 | by ( ) www.reuters.com time to read: +3 min

The approval comes months after the FDA declined to approve expanded use of Acadia's drug Nuplazid to treat psychosis related to Alzheimer's disease. Acadia said it plans to make the drug available to patients by the end of April. He forecast peak U.S. trofinetide sales of $487.2 million by 2035. After the FDA declined to approve the expanded use of Nuplazid, Acadia said it would not pursue that indication for Nuplazid further. Improvement of symptoms was measured according to the assessment scales Rett Syndrome Behaviour Questionnaire and the Clinical Global Impression of Improvement.

☆ U.S. FDA approves Acadia's genetic Rett syndrome drug
▼ + stars: | 2023-03-11 | by ( ) www.reuters.com time to read: +3 min

March 10 (Reuters) - The U.S. Food and Drug Administration approved Acadia Pharmaceuticals Inc's (ACAD.O) drug for the treatment of Rett syndrome, a genetic brain disorder, the company said on Friday, making it the first approved drug for the condition. The approval comes months after the FDA declined to approve expanded use of Acadia's drug Nuplazid to treat psychosis related to Alzheimer's disease. Acadia said it plans to make the drug available to patients by the end of April. He forecast peak U.S. trofinetide sales of $487.2 million by 2035. Improvement of symptoms was measured according to the assessment scales Rett Syndrome Behaviour Questionnaire and the Clinical Global Impression of Improvement.

☆ Kids with 'bubble boy' disease could finally get access to a life-saving gene therapy, as a study starts back up at UCLA
▼ + stars: | 2022-12-27 | by ( Andrew Dunn | ) www.businessinsider.com time to read: +4 min

UCLA researchers are restarting a study to give a gene therapy to kids with an ultra-rare disease. Without gene therapy, doctors treat kids with SCID using enzyme-replacement therapies, if they are ineligible for bone-marrow transplants. In an email to Insider, Kohn said he expects to be able to treat between three and six patients with his current funding. Drug companies have shown little interest in the treatments because the complexity of the treatments and tiny number of eligible patients limit potential profits. Drug companies have deprioritized or shelved gene-therapy programs to treat a range of rare diseases, including Wiskott-Aldrich syndrome, MPS, Batten disease, chronic granulomatous disease, Rett syndrome, and Fabry disease.

Stephen "tWitch" Boss was a thoroughly modern dancer. He lit up the stage of "The Ellen DeGeneres Show" for nearly a decade. He was so classy," Boss told The Associated Press in 2014, the year he joined the "Ellen" show. Stephen "tWitch" Boss on "Ellen's Game of Games." Stephen "tWitch" Boss and Ellen DeGeneres on "Ellen's Game of Games".

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